Skip to main content

Table 4 The frequency of off label use in voxelotor

From: A retrospective research of adverse event reporting system events for voxelotor based on the FAERS database

PT

Number

Percent

Haemoglobin C disease

380

30.7%

Haemolytic anaemia

316

25.5%

Anaemia

172

13.9%

Thalassaemia beta

122

9.9%

Haemoglobin decreased

41

0.3%

Full blood count decreased

27

0.2%

Haemochromatosis

21

0.2%

Pain

22

0.2%

Iron metabolism disorder

13

0.1%

Haemoglobin abnormal

12

0.1%